Three 2026 Breakthrough Prize winners reflect on developing Luxturna, a gene therapy that treats blindness caused by rare ...
An experimental gene therapy for a rare form of genetic deafness has successfully restored hearing in children and adults, ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain disorders known as SYNGAP1-related disorders, or SRDs. Researchers were able ...
Travis Smith was a very serious baby. Born completely unable to hear, his mother, Sierra, struggled to see his personality ...
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have persisted for more than two years for some patients.