For example, using TRACER, Voyager has discovered a series of novel AAV capsids that, following intravenous (IV) administration, achieve up to 1,000-fold higher RNA expression in the brain and 100 ...

Lilly is the third company to partner with Sangamo on STAC-BBB after Astellas Gene Therapies, which paid $20 million upfront ...

Age-related macular degeneration (AMD) is the leading cause of blindness among older adults. The exudative or ‘wet’ form of the disease is characterized by the growth of abnormal blood vessels from ...

Scientists at the Icahn School of Medicine at Mount Sinai have developed a lipid nanoparticle system capable of delivering ...

Qiutang Li’s team uses a recombinant adeno-associated virus (AAV) to deliver the correct ... simplex virus to be administrated via multiple intravenous injections. “The most common route ...